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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
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Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
CaVβs
Muscle Biology
NAD+
Inhibitors
Mitochondrial fission
Dystrophine
Clinical trials
Energy Metabolism/drug effects
BMD
Long noncoding RNA
CaV subunits
Dystrophin central domain
Mdx mouse
Calcium Channels
LKB1
Animals
Long QT
LncRNA
Autophagy
Exon skipping
Gene expression
Muscular dystrophy
Calcium
Humans
Duchenne DMD dystrophy
Muscles/physiopathology
Becker muscular dystrophy
Drp1
DMO
Gene Expression Regulation/drug effects
NNOS
Cell Biology
Duchenne muscular dystrophy DMD
Dystrophin
Becker BMD muscular dystrophy
Multiresolution modeling
Immunoglobulin Fc Fragments/pharmacology
Cardiomyopathie
Myogenesis
Dystrophie Musculaire de Duchenne DMD
Muscular Dystrophy
Muscle development
Duchenne muscular dystrophy
Muscular Atrophy
Morphogenesis
Dystrophie musculaire de Becker
Molecular docking
Gene modifiers
Cell Line
Inbred mdx
Hepatocellular carcinoma
Delivery
Génomique
Molecular Sequence Data
Invivo
Genomic
Animal/physiopathology
Knockout
MiARN
Male
Diseases
Inbred C57BL
Skeletal muscle
Cell homeostasis
Becker muscular dystrophy BMD
Muscle Strength
CTNNB1
LncARN
Cardiomyopathy
DMD
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Dynamin 2
Mice
Base Sequence
Activin Receptors
Multi exon skipping
Cells
Liver
L-Type
Epigenetics
Cultured
Multi resolution modeling
Dystrophy
Homeostasis
Modificateurs de gènes
Antisense oligonucleotides
Cachexia
Muscle
Hear
Ex-vivo
Myotendinous junction
Human Umbilical Vein Endothelial Cells
Dystrophie Musculaire de Becker BMD
Metabolism
DHPR α1S
Dystrophin-EGFP
MES
Centronuclear myopathy
Allele‐specific silencing therapy
CD38